generative
CRISPR Therapy Design Pipeline
End-to-end design of CRISPR therapeutic components: guide RNAs, HDR templates, and safety validation.
CRISPRGene TherapyGuide RNA Design
Input Data
{
"gene": "BRCA1",
"target_locus": "chr17:43044295-43044395",
"therapeutic_goal": "gene_knockout",
"pam_type": "NGG"
}Execution Pipeline
1
Generate Optimized Guide RNAs
/generate_optimized_guide_rna
2
Design HDR Repair Template
/generate_repair_template
3
Validate Guide Efficacy
/predict_crispr_spacer_efficacy