generative

Gene Therapy Vector Optimization

Design tissue-specific regulatory elements and optimize expression for targeted gene therapy.

Gene TherapyAAV VectorsRegulatory Elements

Input Data

{
  "target_tissue": "liver",
  "expression_level": "high",
  "therapeutic_gene": "F9",
  "vector_type": "AAV"
}

Execution Pipeline

1

Design Tissue-Specific Promoter

/generate_regulatory_element

2

Optimize Chromatin Context

/generate_epigenome_sequence

3

Validate Regulatory Function

/predict_chromatin_accessibility