generative
Gene Therapy Vector Optimization
Design tissue-specific regulatory elements and optimize expression for targeted gene therapy.
Gene TherapyAAV VectorsRegulatory Elements
Input Data
{
"target_tissue": "liver",
"expression_level": "high",
"therapeutic_gene": "F9",
"vector_type": "AAV"
}Execution Pipeline
1
Design Tissue-Specific Promoter
/generate_regulatory_element
2
Optimize Chromatin Context
/generate_epigenome_sequence
3
Validate Regulatory Function
/predict_chromatin_accessibility